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Genglycos
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FDA approval of Genglycos for GSDIa
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Latest: FDA approves Genglycos for glycogen storage disease type Ia
The U.S. Food and Drug Administration (FDA) has granted accelerated approval to Ultragenyx Pharmaceutical’s gene therapy, Genglycos (pariglasgene brecaparvovec-opnr). This is the first authorized gene therapy for adult a